Safety through design: Expanding options for spinal muscular atrophy gene therapy

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Original language	English
Article number	101550
Journal	Molecular Therapy Methods and Clinical Development
Volume	33
Issue number	3
DOIs	https://doi.org/10.1016/j.omtm.2025.101550
Publication status	Published - 11 Sept 2025

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title = "Safety through design: Expanding options for spinal muscular atrophy gene therapy",

author = "Groen, \{Ewout J.N.\} and Wadman, \{Renske I.\}",

year = "2025",

month = sep,

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doi = "10.1016/j.omtm.2025.101550",

language = "English",

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journal = "Molecular Therapy Methods and Clinical Development",

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TY - JOUR

T1 - Safety through design

T2 - Expanding options for spinal muscular atrophy gene therapy

AU - Groen, Ewout J.N.

AU - Wadman, Renske I.

PY - 2025/9/11

Y1 - 2025/9/11

UR - https://www.scopus.com/pages/publications/105013356702

U2 - 10.1016/j.omtm.2025.101550

DO - 10.1016/j.omtm.2025.101550

M3 - Comment/Letter to the editor

AN - SCOPUS:105013356702

SN - 2329-0501

VL - 33

JO - Molecular Therapy Methods and Clinical Development

JF - Molecular Therapy Methods and Clinical Development

IS - 3

M1 - 101550

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