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Repositioning 'old' drugs to treat rare diseases: arguing from the mechanism of action

  • Marjolein Drent
  • , Aalt Bast
  • , Hans-Peter Bootsma
  • , Vera Deneer

Research output: Contribution to journalArticleAcademicpeer-review

Original languageEnglish
Pages (from-to)191-194
Number of pages4
JournalSarcoidosis, Vasculitis, and Diffuse Lung Diseases
Volume33
Issue number2
Publication statusPublished - 1 Aug 2016
Externally publishedYes

Keywords

  • Administration, Oral
  • Aminopyridines/administration & dosage
  • Benzamides/administration & dosage
  • Cyclopropanes/administration & dosage
  • Drug Repositioning
  • Evidence-Based Medicine
  • Female
  • Histiocytosis, Langerhans-Cell/diagnosis
  • Humans
  • Middle Aged
  • Orphan Drug Production
  • Phosphodiesterase 4 Inhibitors/administration & dosage
  • Rare Diseases/drug therapy
  • Tomography, X-Ray Computed
  • Treatment Outcome

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