Outcome of haematopoietic cell transplantation in children with lysosomal acid lipase deficiency: a study on behalf of the EBMT Inborn Errors Working Party

Su Han Lum, Milen Minkov, Simon A. Jones, Sheree Hazelaar, Tiarlan Sirait, Jane E. Potter, Polina Stepensky, Frederic Garban, Herbert Pichler, Jerry Stein, Zuhre Kaya, Ansgar Schulz, Karin Mellgren, Cristina Diaz de Heredia, Cecile Pochon, Susana Riesco, Miguel Angel Diaz, Gérard Michel, Caroline Lindemans, Bernd GruhnMichael H. Albert, Arjan C. Lankester, Bénédicte Neven, Robert Wynn*

*Corresponding author for this work

Research output: Contribution to journalLetterAcademicpeer-review

Original languageEnglish
Pages (from-to)594-596
Number of pages3
JournalBone Marrow Transplantation
Volume58
Issue number5
DOIs
Publication statusPublished - May 2023

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