Mitapivat versus Placebo for Pyruvate Kinase Deficiency. Reply

Hanny Al-Samkari, Vanessa Beynon, Eduard J. van Beers

Research output: Contribution to journalComment/Letter to the editorAcademicpeer-review

Original languageEnglish
Pages (from-to)2538-2539
Number of pages2
JournalThe New England journal of medicine
Volume386
Issue number26
DOIs
Publication statusPublished - 30 Jun 2022

Keywords

  • Anemia, Hemolytic, Congenital Nonspherocytic
  • Humans
  • Piperazines
  • Pyruvate Kinase/deficiency
  • Pyruvate Metabolism, Inborn Errors
  • Quinolines

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