@article{dd220fed887644d0b1dbb346fdf50467,
title = "Drug development for exceptionally rare metabolic diseases: challenging but not impossible",
keywords = "Econometric and Statistical Methods: General, Geneeskunde (GENK), Geneeskunde(GENK), Medical sciences, Bescherming en bevordering van de menselijke gezondheid",
author = "M. Putzeist and A.K. Mantel-Teeuwisse and {Gispen-de Wied}, C.C. and A.W. Hoes and H.G.M. Leufkens and R.L.A. Vrueh",
year = "2013",
language = "Undefined/Unknown",
volume = "8",
pages = "179",
journal = "Orphanet Journal of Rare Diseases",
issn = "1750-1172",
publisher = "BioMed Central",
}