Complete correction of enzymatic deficiency and neurochemistry in the GM1-gangliosidosis mouse brain by neonatal adeno-associated virus-mediated gene delivery

Translated title of the contribution: Complete correction of enzymatic deficiency and neurochemistry in the GM1-gangliosidosis mouse brain by neonatal adeno-associated virus-mediated gene delivery

Marieke Broekman, R.C. Baek, L.A. Comer, J.L. Fernandez, T.N. Seyfried, M. Sena-Esteves

Research output: Contribution to journalArticleAcademicpeer-review

Translated title of the contributionComplete correction of enzymatic deficiency and neurochemistry in the GM1-gangliosidosis mouse brain by neonatal adeno-associated virus-mediated gene delivery
Original languageUndefined/Unknown
Pages (from-to)30-37
Number of pages8
JournalMolecular Therapy
Volume15
Issue number1
Publication statusPublished - 2007

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