Clinically meaningful improvements in patient-reported outcomes in mitapivat-treated patients with pyruvate kinase deficiency

Kevin H.M. Kuo*, Rachael F. Grace, Eduard J. van Beers, Wilma Barcellini, Andreas Glenthøj, Susanne Holzhauer, Vanessa Beynon, Susan Morris, Junlong Li, Erin Zagadailov, Parija Patel, Hanny Al-Samkari

*Corresponding author for this work

Research output: Contribution to journalLetterAcademicpeer-review

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Original languageEnglish
Pages (from-to)1415-1419
Number of pages5
JournalAmerican journal of hematology
Volume99
Issue number7
DOIs
Publication statusPublished - Jul 2024

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