| Original language | English |
|---|---|
| Pages (from-to) | 1415-1419 |
| Number of pages | 5 |
| Journal | American journal of hematology |
| Volume | 99 |
| Issue number | 7 |
| DOIs | |
| Publication status | Published - Jul 2024 |
Clinically meaningful improvements in patient-reported outcomes in mitapivat-treated patients with pyruvate kinase deficiency
Kevin H.M. Kuo*, Rachael F. Grace, Eduard J. van Beers, Wilma Barcellini, Andreas Glenthøj, Susanne Holzhauer, Vanessa Beynon, Susan Morris, Junlong Li, Erin Zagadailov, Parija Patel, Hanny Al-Samkari
*Corresponding author for this work
Research output: Contribution to journal › Letter › Academic › peer-review
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