CFTR Function Restoration upon Elexacaftor/Tezacaftor/Ivacaftor Treatment in Patient-Derived Intestinal Organoids with Rare CFTR Genotypes.
Juliet W Lefferts, Marlou C Bierlaagh, Suzanne Kroes, Natascha D A Nieuwenhuijze, Heleen N Sonneveld van Kooten, Paul J Niemöller, Tibo F Verburg, Hettie M Janssens, Danya Muilwijk, Sam F B van Beuningen, Cornelis K van der Ent, Jeffrey M Beekman
Research output: Contribution to journal › Article › Academic › peer-review
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