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Ataluren for the treatment of nonsense-mutation cystic fibrosis: a randomised, double-blind, placebo-controlled phase 3 trial.

  • E. Kerem
  • , M. W. Konstan
  • , [No Value] et al
  • , I. Bronsveld
  • , X. Cystic Fibrosis Ataluren Study Group
  • , S.M. Rowe

Research output: Contribution to journalArticleAcademicpeer-review

Original languageEnglish
Pages (from-to)539-547
Number of pages9
JournalThe Lancet Respiratory Medicine
Volume2
Issue number7
Publication statusPublished - 2014

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