AAV-mediated gene delivery in adult GM1-gangliosidosis mice corrects lysosomal storage in CNS and improves survival

Translated title of the contribution: AAV-mediated gene delivery in adult GM1-gangliosidosis mice corrects lysosomal storage in CNS and improves survival

R.C. Baek, Marieke Broekman, S.G. LeRoy, L.A. Tierney, M.A. Sandberg, A. d'Azzo, T.N. Seyfried, M. Sena-Esteves

Research output: Contribution to journalArticleAcademicpeer-review

Translated title of the contributionAAV-mediated gene delivery in adult GM1-gangliosidosis mice corrects lysosomal storage in CNS and improves survival
Original languageUndefined/Unknown
Pages (from-to)e13468
Number of pages1
JournalPLoS ONE [E]
Volume5
Issue number10
Publication statusPublished - 2010

Keywords

  • Econometric and Statistical Methods: General
  • Geneeskunde (GENK)
  • Geneeskunde(GENK)
  • Medical sciences
  • Bescherming en bevordering van de menselijke gezondheid

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